Ruggieri, Margherita

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Journal Article

Nizzardo, Monica; Simone, Chiara; Salani, Sabrina; Ruepp, Marc-David; Rizzo, Federica; Ruggieri, Margherita; Zanetta, Chiara; Brajkovic, Simona; Moulton, Hong M.; Mühlemann, Oliver; Bresolin, Nereo; Comi, Giacomo P.; Corti, Stefania (2014). Effect of Combined Systemic and Local Morpholino Treatment on the Spinal Muscular Atrophy Δ7 Mouse Model Phenotype. Clinical therapeutics, 36(3), 340-356.e5. Elsevier 10.1016/j.clinthera.2014.02.004

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