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Imbert, Marine; Blandel, Florence; Leumann, Christian; Garcia, Luis; Goyenvalle, Aurelie (2019). Lowering Mutant Huntingtin Using Tricyclo-DNA Antisense Oligonucleotides As a Therapeutic Approach for Huntington's Disease. Nucleic acid therapeutics, 29(5), pp. 256-265. Mary Ann Liebert 10.1089/nat.2018.0775
Robin, Valérie; Griffith, Graziella; Carter, John-Paul L.; Leumann, Christian; Garcia, Luis; Goyenvalle, Aurélie (2017). Efficient SMN Rescue following Subcutaneous Tricyclo-DNA Antisense Oligonucleotide Treatment. Molecular Therapy - Nucleic Acids, 7, pp. 81-89. Nature Publishing Group 10.1016/j.omtn.2017.02.009
Relizani, Karima; Griffith, Graziella; Echevarría, Lucía; Zarrouki, Faouzi; Facchinetti, Patricia; Vaillend, Cyrille; Leumann, Christian; Garcia, Luis; Goyenvalle, Aurélie (2017). Efficacy and Safety Profile of Tricyclo-DNA Antisense Oligonucleotides in Duchenne Muscular Dystrophy Mouse Model. Molecular Therapy - Nucleic Acids, 8, pp. 144-157. Nature Publishing Group 10.1016/j.omtn.2017.06.013
Goyenvalle, Aurelie; Leumann, Christian; Garcia, Luis (2016). Therapeutic Potential of Tricyclo-DNA antisense oligonucleotides. Journal of neuromuscular diseases, 3(2), pp. 157-167. IOS Press 10.3233/jnd-160146
Goyenvalle, Aurelie; Griffith, Graziella; Babbs, Arran; Andaloussi, Samir El; Ezzat, Kariem; Avril, Aurelie; Dugovic, Branislav; Chaussenot, Remi; Ferry, Arnaud; Voit, Thomas; Amthor, Helge; Bühr, Claudia; Schürch, Stefan; Wood, Matthew J. A.; Davies, Kay E.; Vaillend, Cyrille; Leumann, Christian; Garcia, Luis (2015). Functional correction in mouse models of muscular dystrophy using exon-skipping tricyclo-DNA oligomers. Nature medicine, 21(3), pp. 270-275. Nature Publishing Group 10.1038/nm.3765
Robin, Valerie; Ittig, Damian; Voit, Thomas; Leumann, Christian J.; Garcia, Luis (22 October 2012). SMN rescue by using oligonucleotides of tricyclo-DNA to induce exon 7 inclusion in SMN2 mRNA. Human gene therapy, 23(10), A37-A38. Mary Ann Liebert Inc.
